Orchard Therapeutics Global Website

Grow beyond

Opening up possibilities for people with rare inherited diseases

Cecilia

Born with metachromatic leukodystrophy

Inspiration and impact

At Orchard, we measure our impact in lifetimes. Read more about our commitment to sustaining communities and hear the stories that inspire us and ignite our imagination.

Families

Pioneering science

We’re building on decades of research to develop potential cures. Learn how our ex vivo gene therapy technology is designed to work and explore our pipeline.

About gene therapy

Clinical trials

To read information on our clinical trial programme, please click below

Clinical trials